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Access Programs for Miglustat

Drug Company Assistance

Actelion Pharmaceuticals US, Inc. has a patient support program for patients taking miglustat. At this time, however, the drug manufacturer does not have a program to help patients access the medication at reduced costs. If you know of such a program, please contact ASH Policy and Practice Associate, Katherine Stark.

Foundation Assistance

The National Gaucher Care Foundation, Inc. provides a range of resources for people diagnosed with Gaucher Disease. Please use their online application, email [email protected], or call 1-866-346-8176 for more information regarding eligibility and enrollment.